A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease, GM1 Gangliosidosis or GM2 Gangliosidosis
PHASE3
An 18-month double-blind, randomized, placebo-controlled, multicenter, Phas...
Status
Recruiting
Location
UCSF Children's Hospital and Research Center at Oakland
Samotolisib in Treating Patients With Relapsed or Refractory Advanced Solid Tumors, Non-Hodgkin Lymphoma, or Histiocytic Disorders With TSC or PI3K/MTOR Mutations (A Pediatric MATCH Treatment Trial)
PHASE2
This phase II Pediatric MATCH trial studies how well samotolisib works in t...
Targeted Therapy Directed by Genetic Testing in Treating Patients With Advanced Refractory Solid Tumors, Lymphomas, or Multiple Myeloma (The MATCH Screening Trial)
PHASE2
This phase II MATCH screening and multi-sub-trial studies how well treatmen...
Anvumetostat Alone or in Combination With Other Therapies in Subjects With Advanced Thoracic Tumors With Homozygous MTAP-deletion (Master Protocol) (MTAPESTRY 104).
PHASE1
The study aims to determine maximum tolerated dose (MTD) or recommended com...
Targeted Therapy Directed by Genetic Testing in Treating Pediatric Patients With Relapsed or Refractory Advanced Solid Tumors, Non-Hodgkin Lymphomas, or Histiocytic Disorders (The Pediatric MATCH Screening Trial)
PHASE2
This phase II Pediatric MATCH screening and multi-sub-trial studies how wel...